Found 5 results
Filters: Keyword is Gene Editing  [Clear All Filters]
2018
Long J, Hoban MD, Cooper AR, Kaufman ML, Kuo CY, Campo-Fernandez B, Lumaquin D, Hollis RP, Wang X, Kohn DB et al..  2018.  Characterization of Gene Alterations following Editing of the β-Globin Gene Locus in Hematopoietic Stem/Progenitor Cells.. Mol Ther. 26(2):468-479.
Zafra MPaz, Schatoff EM, Katti A, Foronda M, Breinig M, Schweitzer AY, Simon A, Han T, Goswami S, Montgomery E et al..  2018.  Optimized base editors enable efficient editing in cells, organoids and mice.. Nat Biotechnol. 36(9):888-893.
2017
Shi Z-D, Lee K, Yang D, Amin S, Verma N, Li QV, Zhu Z, Soh C-L, Kumar R, Evans T et al..  2017.  Genome Editing in hPSCs Reveals GATA6 Haploinsufficiency and a Genetic Interaction with GATA4 in Human Pancreatic Development.. Cell Stem Cell. 20(5):675-688.e6.
O'Rourke KP, Loizou E, Livshits G, Schatoff EM, Baslan T, Manchado E, Simon J, Romesser PB, Leach B, Han T et al..  2017.  Transplantation of engineered organoids enables rapid generation of metastatic mouse models of colorectal cancer.. Nat Biotechnol. 35(6):577-582.
2016
Hoban MD, Lumaquin D, Kuo CY, Romero Z, Long J, Ho M, Young CS, Mojadidi M, Fitz-Gibbon S, Cooper AR et al..  2016.  CRISPR/Cas9-Mediated Correction of the Sickle Mutation in Human CD34+ cells.. Mol Ther. 24(9):1561-9.